U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
rebisufligene etisparvovec [INN]
Preferred Name English
Rebisufligene Etisparvovec
INN  
Official Name English
DNA (synthetic adeno-associated virus 9 vector scAAV9.U1a.hSGSH human N-Sulfoglucosamine sulfohydrolase-specifying)
Common Name English
UX111
Code English
ABO-102
Common Name English
SCAAV9.U1A.HSGSH
Code English
Non-replicating, self-complementary, and recombinant adeno-associated virus (AAV) serotype 9 viral vector encoding a functional variant of the human N-sulfoglucosamine sulfohydrolase (hSGSH) transgene
Common Name English
UX-111
Code English
REBISUFLIGENE ETISPARVOVEC [USAN]
Common Name English
Classification Tree Code System Code
FDA ORPHAN DRUG 433714
Created by admin on Wed Apr 02 06:17:37 GMT 2025 , Edited by admin on Wed Apr 02 06:17:37 GMT 2025
Code System Code Type Description
INN
10697
Created by admin on Wed Apr 02 06:17:37 GMT 2025 , Edited by admin on Wed Apr 02 06:17:37 GMT 2025
PRIMARY
USAN
MN-59
Created by admin on Wed Apr 02 06:17:37 GMT 2025 , Edited by admin on Wed Apr 02 06:17:37 GMT 2025
PRIMARY
SMS_ID
100000181385
Created by admin on Wed Apr 02 06:17:37 GMT 2025 , Edited by admin on Wed Apr 02 06:17:37 GMT 2025
PRIMARY
NCI_THESAURUS
C171802
Created by admin on Wed Apr 02 06:17:37 GMT 2025 , Edited by admin on Wed Apr 02 06:17:37 GMT 2025
PRIMARY
CAS
1966978-67-5
Created by admin on Wed Apr 02 06:17:37 GMT 2025 , Edited by admin on Wed Apr 02 06:17:37 GMT 2025
PRIMARY
FDA UNII
V28L3Q0LVZ
Created by admin on Wed Apr 02 06:17:37 GMT 2025 , Edited by admin on Wed Apr 02 06:17:37 GMT 2025
PRIMARY