U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
A RECOMBINANT REPLICATION-DEFECTIVE ADENO-ASSOCIATED VIRAL VECTOR SEROTYPE 8 (RAAV8) ENCODING CODON-OPTIMISED HUMAN RETINITIS PIGMENTOSA GTPASE REGULATOR (RPGR), UNDER THE CONTROL OF HUMAN RHODOPSIN KINASE (RK) PROMOTER AND BOVINE GROWTH HORMONE POLY(A)
Preferred Name English
COTORETIGENE TOLIPARVOVEC
INN   USAN  
Official Name English
RECOMBINANT SEROTYPE 8 ADENO-ASSOCIATED VIRAL VECTOR (AAV8) ENCODING A CODON OPTIMISED (CO) COPY OF THE CDNA ENCODING HUMAN RETINITIS PIGMENTOSA GTPASE REGULATOR (CORPGR)
Common Name English
AAV8-RPGR
Common Name English
cotoretigene toliparvovec [INN]
Common Name English
COTORETIGENE TOLIPARVOVEC [USAN]
Common Name English
Code System Code Type Description
INN
11358
Created by admin on Wed Apr 02 10:53:22 GMT 2025 , Edited by admin on Wed Apr 02 10:53:22 GMT 2025
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SMS_ID
100000181881
Created by admin on Wed Apr 02 10:53:22 GMT 2025 , Edited by admin on Wed Apr 02 10:53:22 GMT 2025
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FDA UNII
V1R4T1S1M0
Created by admin on Wed Apr 02 10:53:22 GMT 2025 , Edited by admin on Wed Apr 02 10:53:22 GMT 2025
PRIMARY
CAS
2246424-95-1
Created by admin on Wed Apr 02 10:53:22 GMT 2025 , Edited by admin on Wed Apr 02 10:53:22 GMT 2025
PRIMARY
NCI_THESAURUS
C177095
Created by admin on Wed Apr 02 10:53:22 GMT 2025 , Edited by admin on Wed Apr 02 10:53:22 GMT 2025
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USAN
GH-110
Created by admin on Wed Apr 02 10:53:22 GMT 2025 , Edited by admin on Wed Apr 02 10:53:22 GMT 2025
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