U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
COTORETIGENE TOLIPARVOVEC
INN   USAN  
Official Name English
RECOMBINANT SEROTYPE 8 ADENO-ASSOCIATED VIRAL VECTOR (AAV8) ENCODING A CODON OPTIMISED (CO) COPY OF THE CDNA ENCODING HUMAN RETINITIS PIGMENTOSA GTPASE REGULATOR (CORPGR)
Common Name English
AAV8-RPGR
Common Name English
A RECOMBINANT REPLICATION-DEFECTIVE ADENO-ASSOCIATED VIRAL VECTOR SEROTYPE 8 (RAAV8) ENCODING CODON-OPTIMISED HUMAN RETINITIS PIGMENTOSA GTPASE REGULATOR (RPGR), UNDER THE CONTROL OF HUMAN RHODOPSIN KINASE (RK) PROMOTER AND BOVINE GROWTH HORMONE POLY(A)
Common Name English
cotoretigene toliparvovec [INN]
Common Name English
COTORETIGENE TOLIPARVOVEC [USAN]
Common Name English
Code System Code Type Description
INN
11358
Created by admin on Sat Dec 16 18:22:10 UTC 2023 , Edited by admin on Sat Dec 16 18:22:10 UTC 2023
PRIMARY
FDA UNII
V1R4T1S1M0
Created by admin on Sat Dec 16 18:22:10 UTC 2023 , Edited by admin on Sat Dec 16 18:22:10 UTC 2023
PRIMARY
CAS
2246424-95-1
Created by admin on Sat Dec 16 18:22:10 UTC 2023 , Edited by admin on Sat Dec 16 18:22:10 UTC 2023
PRIMARY
NCI_THESAURUS
C177095
Created by admin on Sat Dec 16 18:22:10 UTC 2023 , Edited by admin on Sat Dec 16 18:22:10 UTC 2023
PRIMARY
USAN
GH-110
Created by admin on Sat Dec 16 18:22:10 UTC 2023 , Edited by admin on Sat Dec 16 18:22:10 UTC 2023
PRIMARY