U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
139594
Name Type Language
ZAFTUCLENEGENE PIRUPARVOVEC
INN  
Official Name English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR TSHA-118 CHICKEN .BETA.-ACTIN HYBRID PROMOTER PLUS HUMAN ACYL PROTEIN THIOESTER HYDROLASE PPT1 PRECURSOR TRANSGENE PLUS BOVINE GROWTH HORMONE POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 9 INVERTED TER
Common Name English
zaftuclenegene piruparvovec [INN]
Common Name English
RECOMBINANT, SELF-COMPLEMENTARY (DIMERIC), NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (SCAAV9) VECTOR, ENCODING CODON-OPTIMISED HUMAN PALMITOYL-PROTEIN THIOESTERASE 1 (PPT1, CLN1), UNDER THE CONTROL OF A SYNTHETIC PROMOTER CONSISTING OF ACYTOMEGAL
Common Name English
Code System Code Type Description
FDA UNII
R5X46L79RV
Created by admin on Sat Dec 16 18:10:02 GMT 2023 , Edited by admin on Sat Dec 16 18:10:02 GMT 2023
PRIMARY
INN
12046
Created by admin on Sat Dec 16 18:10:02 GMT 2023 , Edited by admin on Sat Dec 16 18:10:02 GMT 2023
PRIMARY
NCI_THESAURUS
C188620
Created by admin on Sat Dec 16 18:10:02 GMT 2023 , Edited by admin on Sat Dec 16 18:10:02 GMT 2023
PRIMARY
CAS
2567881-78-9
Created by admin on Sat Dec 16 18:10:02 GMT 2023 , Edited by admin on Sat Dec 16 18:10:02 GMT 2023
PRIMARY
NIH
NCATS
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