Recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector encoding human adenosine triphosphate (ATP)-binding cassette sub-family D member 1 (ABCD1, also known as adrenoleukodystrophy (ALD) protein) under control of a human cytomegalo
Common Name
English
DNA (recombinant replication-defective adeno-associated virus serotype 9 vector SBT101 cytomegalovirus enhancer fusion with chicken ?-actin promoter and exon 1plus chimeric chicken ?-actin and rabbit ?-globin intron plus rabbit ?-globin exon 3 plus 5?-un