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Approval Year

Unknown
149124
Name Type Language
Pozetaldogene Ormesparvovec
INN  
Official Name English
SBT-101
Preferred Name English
Recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector encoding human adenosine triphosphate (ATP)-binding cassette sub-family D member 1 (ABCD1, also known as adrenoleukodystrophy (ALD) protein) under control of a human cytomegalo
Common Name English
DNA (recombinant replication-defective adeno-associated virus serotype 9 vector SBT101 cytomegalovirus enhancer fusion with chicken ?-actin promoter and exon 1plus chimeric chicken ?-actin and rabbit ?-globin intron plus rabbit ?-globin exon 3 plus 5?-un
Common Name English
POZETALDOGENE ORMESPARVOVEC [USAN]
Common Name English
SBT101
Code English
pozetaldogene ormesparvovec [INN]
Common Name English
Code System Code Type Description
CAS
2764626-03-9
Created by admin on Wed Apr 02 18:50:28 GMT 2025 , Edited by admin on Wed Apr 02 18:50:28 GMT 2025
PRIMARY
USAN
MN-234
Created by admin on Wed Apr 02 18:50:28 GMT 2025 , Edited by admin on Wed Apr 02 18:50:28 GMT 2025
PRIMARY
INN
12672
Created by admin on Wed Apr 02 18:50:28 GMT 2025 , Edited by admin on Wed Apr 02 18:50:28 GMT 2025
PRIMARY
FDA UNII
R5CJD8SH2N
Created by admin on Wed Apr 02 18:50:28 GMT 2025 , Edited by admin on Wed Apr 02 18:50:28 GMT 2025
PRIMARY
SMS_ID
300000043620
Created by admin on Wed Apr 02 18:50:28 GMT 2025 , Edited by admin on Wed Apr 02 18:50:28 GMT 2025
PRIMARY
NCI_THESAURUS
C203115
Created by admin on Wed Apr 02 18:50:28 GMT 2025 , Edited by admin on Wed Apr 02 18:50:28 GMT 2025
PRIMARY
NIH
NCATS
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