U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
DYN-101
Code English
DYNAMIN 101
Preferred Name English
IONIS-DNM2-2.5RX
Common Name English
DYNAMIN-101
Code English
Classification Tree Code System Code
EU-Orphan Drug EU/3/19/2171
Created by admin on Wed Apr 02 08:33:22 GMT 2025 , Edited by admin on Wed Apr 02 08:33:22 GMT 2025
FDA ORPHAN DRUG 702819
Created by admin on Wed Apr 02 08:33:22 GMT 2025 , Edited by admin on Wed Apr 02 08:33:22 GMT 2025
Code System Code Type Description
FDA UNII
NZL8REY4K6
Created by admin on Wed Apr 02 08:33:22 GMT 2025 , Edited by admin on Wed Apr 02 08:33:22 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_4-1_13 10 / 16
1_1-1_3;1_14-1_16 6 / 16
Linkage Site Range Site Count
Sodium Phosporothioate 1_2-1_16 15 / 15