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Approval Year

Unknown
149124
Name Type Language
TSHA-102
Preferred Name English
Lonimecgene Renparvovec
INN   USAN  
Official Name English
LONIMECGENE RENPARVOVEC [USAN]
Common Name English
recombinant, self-complementary (dimeric), non-replicating adeno-associated virus serotype 9 (scAAV9) vector encoding a miniaturised form of human methyl-CpG binding protein 2 (MECP2) containing the methyl-CpG-binding domain (MBD) and the NCoR/SMRT (sile
Common Name English
lonimecgene renparvovec [INN]
Common Name English
DNA (self-complementary adeno-associated virus 9 vector TSHA-102 mouse neuronal-specific promoter MeP426 variant plus human gene MECP2 fragment plus microRNA-binding element RDH1pA plus miRARE (miRNA responsive auto-regulatory element) plus human gene ME
Common Name English
Code System Code Type Description
SMS_ID
300000032082
Created by admin on Wed Apr 02 19:41:41 GMT 2025 , Edited by admin on Wed Apr 02 19:41:41 GMT 2025
PRIMARY
FDA UNII
NVK87P6NXW
Created by admin on Wed Apr 02 19:41:41 GMT 2025 , Edited by admin on Wed Apr 02 19:41:41 GMT 2025
PRIMARY
INN
12970
Created by admin on Wed Apr 02 19:41:41 GMT 2025 , Edited by admin on Wed Apr 02 19:41:41 GMT 2025
PRIMARY
CAS
2856375-48-7
Created by admin on Wed Apr 02 19:41:41 GMT 2025 , Edited by admin on Wed Apr 02 19:41:41 GMT 2025
PRIMARY
NCI_THESAURUS
C206935
Created by admin on Wed Apr 02 19:41:41 GMT 2025 , Edited by admin on Wed Apr 02 19:41:41 GMT 2025
PRIMARY
USAN
MN-246
Created by admin on Wed Apr 02 19:41:41 GMT 2025 , Edited by admin on Wed Apr 02 19:41:41 GMT 2025
PRIMARY
NIH
NCATS
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