U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

2022
324
Name Type Language
ZYNTEGLO
Preferred Name English
BETIBEGLOGENE AUTOTEMCEL
USAN   INN  
Official Name English
AUTOLOGOUS CD34+ CELLS ENCODING .BETA.A-T87Q-GLOBIN GENE
Common Name English
BB-305
Code English
betibeglogene autotemcel [INN]
Common Name English
AUTOLOGOUS CD34+ ENRICHED CELL POPULATION THAT CONTAINS HEMATOPOIETIC STEM CELLS (HSC'S) TRANSDUCED WITH THE LENTIGLOBIN BB305 LENTIVIRAL VECTOR (LVV) ENCODING FOR THE .BETA.A-T87Q-GLOBIN GENE. THE CD34+ ENRICHED CELL POPULATION CONTAINING HEMATOPOIETIC
Common Name English
autologous CD34+ hematopoietic stem cells obtained from mobilised peripheral blood of patients with beta-thalassemia, transduced ex vivo with betibeglogene darolentivec (116)(78), a self-inactivating human immunodeficiency virus-1 (HIV-1)-derived lentivi
Common Name English
Betibeglogene autotemcel [WHO-DD]
Common Name English
LENTIGLOBIN BB305
Code English
BETIBEGLOGENE AUTOTEMCEL [USAN]
Common Name English
Classification Tree Code System Code
FDA ORPHAN DRUG 390513
Created by admin on Wed Apr 02 04:59:09 GMT 2025 , Edited by admin on Wed Apr 02 04:59:09 GMT 2025
Code System Code Type Description
DAILYMED
MEE8487RTP
Created by admin on Wed Apr 02 04:59:09 GMT 2025 , Edited by admin on Wed Apr 02 04:59:09 GMT 2025
PRIMARY
INN
10900
Created by admin on Wed Apr 02 04:59:09 GMT 2025 , Edited by admin on Wed Apr 02 04:59:09 GMT 2025
PRIMARY
USAN
GH-155
Created by admin on Wed Apr 02 04:59:09 GMT 2025 , Edited by admin on Wed Apr 02 04:59:09 GMT 2025
PRIMARY
FDA UNII
MEE8487RTP
Created by admin on Wed Apr 02 04:59:09 GMT 2025 , Edited by admin on Wed Apr 02 04:59:09 GMT 2025
PRIMARY
WIKIPEDIA
Zynteglo
Created by admin on Wed Apr 02 04:59:09 GMT 2025 , Edited by admin on Wed Apr 02 04:59:09 GMT 2025
PRIMARY
RXCUI
2610349
Created by admin on Wed Apr 02 04:59:09 GMT 2025 , Edited by admin on Wed Apr 02 04:59:09 GMT 2025
PRIMARY
NCI_THESAURUS
C123881
Created by admin on Wed Apr 02 04:59:09 GMT 2025 , Edited by admin on Wed Apr 02 04:59:09 GMT 2025
PRIMARY
SMS_ID
100000178156
Created by admin on Wed Apr 02 04:59:09 GMT 2025 , Edited by admin on Wed Apr 02 04:59:09 GMT 2025
PRIMARY
NIH
NCATS
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National Center for Advancing Translational Sciences (NCATS),
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