U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
DNA, D((2'-O-(2-METHOXYETHYL))M5RU-SP-(2'-O-(2-METHOXYETHYL))RG-(2'-O-(2-METHOXYETHYL))M5RC-(2'-O-(2-METHOXYETHYL))M5RU-(2'-O-(2-METHOXYETHYL))M5RC-M5C-SP-G-SP-T-SP-T-SP-G-SP-G-SP-T-SP-G-SP-M5C-SP-T-SP-(2'-O-(2-METHOXYETHYL))M5RU-(2'-O-(2-METHOXYETHYL))R
Preferred Name English
PELACARSEN
USAN   INN  
Official Name English
ISIS-681257 (GALNAC3--CONJUGATED ASO TARGETING HUMAN LIPOPROTEIN (A)) FREE ACID
Common Name English
ALL-P-AMBO-5-O-(((6-(5-((TRIS(3-(6-(2-ACETAMIDO-2-DEOXY-.BETA.-D-GALACTOPYRANOSYLOXY)HEXYLAMINO)-3-OXOPROPOXYMETHYL))METHYL)AMINO-5-OXOPENTANAMIDO)HEXOXY))PHOSPHO)-2-O-(2-METHOXYETHYL)-5-METHYL-P-THIOURIDYLYL-(3-O->5-O)-2-O-(2-METHOXYETHYL)GUANYLYL-(3-O-
Common Name English
AKCEA-APO(A)-LRX
Common Name English
Pelacarsen [WHO-DD]
Common Name English
PELACARSEN [USAN]
Common Name English
IONIS-APO(A)-LRX
Common Name English
pelacarsen [INN]
Common Name English
ISIS-681257 FREE ACID
Code English
Code System Code Type Description
FDA UNII
LSO9H7UZ90
Created by admin on Tue Apr 01 21:10:16 GMT 2025 , Edited by admin on Tue Apr 01 21:10:16 GMT 2025
PRIMARY
CAS
1637637-70-7
Created by admin on Tue Apr 01 21:10:16 GMT 2025 , Edited by admin on Tue Apr 01 21:10:16 GMT 2025
PRIMARY
NCI_THESAURUS
C174676
Created by admin on Tue Apr 01 21:10:16 GMT 2025 , Edited by admin on Tue Apr 01 21:10:16 GMT 2025
PRIMARY
INN
11187
Created by admin on Tue Apr 01 21:10:16 GMT 2025 , Edited by admin on Tue Apr 01 21:10:16 GMT 2025
PRIMARY
SMS_ID
100000184297
Created by admin on Tue Apr 01 21:10:16 GMT 2025 , Edited by admin on Tue Apr 01 21:10:16 GMT 2025
PRIMARY
USAN
FG-172
Created by admin on Tue Apr 01 21:10:16 GMT 2025 , Edited by admin on Tue Apr 01 21:10:16 GMT 2025
PRIMARY
CAS
1637639-99-6
Created by admin on Tue Apr 01 21:10:16 GMT 2025 , Edited by admin on Tue Apr 01 21:10:16 GMT 2025
ALTERNATIVE
Sugar Site Range Site Count
Deoxyribose (DNA) 1_7-1_15 9 / 20
2'-O-Methoxyethyl ribose 1_1-1_6;1_16-1_20 11 / 20
Linkage Site Range Site Count
Phosporothioate 1_2;1_7-1_16;1_20 12 / 19
Phosphate 1_3-1_6;1_17-1_19 7 / 19