Capsomere, recombinant adeno-associated virus 5 viral capsid protein VP1-VP2-VP3 complex (1:1:10), hexacontamer, complex with DNA (recombinant adeno-associated virus vector pAAV-hFIXco-v2 Mus musculus transtyretin gene promoter plus human ?-globin gene i
Preferred Name
English
Arvenacogene Sanparvovec
Official Name
English
recombinant non-replicating adeno-associated virus serotype 5 (AAV5) vector encoding a codon-optimized gain of function variant (Padua variant, R338L) of human coagulation factor IX (FIX), under the control of a murine liver-specific transthyretin (TTR)
