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Approval Year

Unknown
149124
Name Type Language
Capsomere, recombinant adeno-associated virus 5 viral capsid protein VP1-VP2-VP3 complex (1:1:10), hexacontamer, complex with DNA (recombinant adeno-associated virus vector pAAV-hFIXco-v2 Mus musculus transtyretin gene promoter plus human ?-globin gene i
Preferred Name English
Arvenacogene Sanparvovec
INN  
Official Name English
recombinant non-replicating adeno-associated virus serotype 5 (AAV5) vector encoding a codon-optimized gain of function variant (Padua variant, R338L) of human coagulation factor IX (FIX), under the control of a murine liver-specific transthyretin (TTR)
Common Name English
arvenacogene sanparvovec [INN]
Common Name English
Code System Code Type Description
NCI_THESAURUS
C211781
Created by admin on Wed Apr 02 20:19:51 GMT 2025 , Edited by admin on Wed Apr 02 20:19:51 GMT 2025
PRIMARY
CAS
2891724-48-2
Created by admin on Wed Apr 02 20:19:51 GMT 2025 , Edited by admin on Wed Apr 02 20:19:51 GMT 2025
PRIMARY
FDA UNII
KNP55LBJ2N
Created by admin on Wed Apr 02 20:19:51 GMT 2025 , Edited by admin on Wed Apr 02 20:19:51 GMT 2025
PRIMARY
INN
13234
Created by admin on Wed Apr 02 20:19:51 GMT 2025 , Edited by admin on Wed Apr 02 20:19:51 GMT 2025
PRIMARY
NIH
NCATS
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