U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
LADEMIRSEN
INN   USAN  
Official Name English
RG-456070
Code English
RG-012
Code English
lademirsen [INN]
Common Name English
ALL-P-AMBO-2'-O-(2-METHOXYETHYL)-P-THIOADENYLYL-(3'->5')-2'-O,4'-C-((1S)-ETHANE-1,1-DIYL)-P-THIOCYTIDYLYL-(3'->5')-2'-DEOXY-P-THIOADENYLYL-(3'->5')-P-THIOTHYMIDYLYL-(3'->5')-2'-O,4'-C-((1S)-ETHANE-1,1-DIYL)-P-THIOCYTIDYLYL-(3'->5')-2'-DEOXY-P-THIOADENYLY
Systematic Name English
SAR-339375
Common Name English
LADEMIRSEN [USAN]
Common Name English
DNA, D(P-THIO)((2'-O-(2-METHOXYETHYL))RA-(3'->4')-(2',5'-ANHYDRO-6'-DEOXY-4'-C-(HYDROXYMETHYL)-.ALPHA.-L-MANNOFURANO)C-A-T-(3'->4')-(2',5'-ANHYDRO-6'-DEOXY-4'-C-(HYDROXYMETHYL)-.ALPHA.-L-MANNOFURANO)C-A-G-T-(3'->4')-(2',5'-ANHYDRO-6'-DEOXY-4'-C-(HYDROXYM
Systematic Name English
DNA, D(P-THIO)((2'-O-(2-METHOXYETHYL))RA-(2'-O,4'-C-((S)-ETHYLIDENE))RC-A-T-(2'-O,4'-C-((S)-ETHYLIDENE))RC-A-G-T-(2'-O,4'-C-((S)-ETHYLIDENE))RC-T-G-A-(2'-O,4'-C-((S)-ETHYLIDENE))RU-A-A-G-(2'-O,4'-C-((S)-ETHYLIDENE))RC-T-(2'-O-(2-METHOXYETHYL))RA)
Common Name English
Code System Code Type Description
INN
10800
Created by admin on Sat Dec 16 15:07:42 UTC 2023 , Edited by admin on Sat Dec 16 15:07:42 UTC 2023
PRIMARY
NCI_THESAURUS
C170089
Created by admin on Sat Dec 16 15:07:42 UTC 2023 , Edited by admin on Sat Dec 16 15:07:42 UTC 2023
PRIMARY
CAS
1404019-95-9
Created by admin on Sat Dec 16 15:07:42 UTC 2023 , Edited by admin on Sat Dec 16 15:07:42 UTC 2023
PRIMARY
FDA UNII
KKQ6AQN9LH
Created by admin on Sat Dec 16 15:07:42 UTC 2023 , Edited by admin on Sat Dec 16 15:07:42 UTC 2023
PRIMARY
USAN
DE-172
Created by admin on Sat Dec 16 15:07:42 UTC 2023 , Edited by admin on Sat Dec 16 15:07:42 UTC 2023
PRIMARY
Sugar Site Range Site Count
2'-O,4'-ethylene bridged Ribose 1_2;1_5;1_9;1_13;1_17 5 / 19
2'-O-Methoxyethyl ribose 1_1;1_19 2 / 19
Deoxyribose (DNA) 1_3-1_4;1_6-1_8;1_10-1_12;1_14-1_16;1_18 12 / 19
Linkage Site Range Site Count
Phosporothioate 1_2-1_19 18 / 18