U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
149124
Name Type Language
Clemidsogene Lanparvovec
USAN   INN  
Official Name English
RGX-121
Preferred Name English
Recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector encoding human iduronate 2-sulfatase (IDS, ?-L-iduronate sulfate sulfatase) under control of a human cytomegalovirus (CMV) immediate-early enhancer/chicken ?-actin (CBA) promot
Common Name English
CLEMIDSOGENE LANPARVOVEC [USAN]
Common Name English
clemidsogene lanparvovec [INN]
Common Name English
DNA (recombinant replication-defective adeno-associated virus 9 vector RGX-121 cytomegalovirus immediate-early promoter-enhancer plus chicken ?-actin promoter plus chicken ?-actin intron plus human iduronate-2-sulfatase gene plus rabbit ?-globin polyaden
Common Name English
Code System Code Type Description
SMS_ID
300000001341
Created by admin on Wed Apr 02 07:50:18 GMT 2025 , Edited by admin on Wed Apr 02 07:50:18 GMT 2025
PRIMARY
CAS
2766142-50-9
Created by admin on Wed Apr 02 07:50:18 GMT 2025 , Edited by admin on Wed Apr 02 07:50:18 GMT 2025
PRIMARY
FDA UNII
K5LW2WBP48
Created by admin on Wed Apr 02 07:50:18 GMT 2025 , Edited by admin on Wed Apr 02 07:50:18 GMT 2025
PRIMARY
NCI_THESAURUS
C203113
Created by admin on Wed Apr 02 07:50:18 GMT 2025 , Edited by admin on Wed Apr 02 07:50:18 GMT 2025
PRIMARY
INN
12682
Created by admin on Wed Apr 02 07:50:18 GMT 2025 , Edited by admin on Wed Apr 02 07:50:18 GMT 2025
PRIMARY
USAN
MN-159
Created by admin on Wed Apr 02 07:50:18 GMT 2025 , Edited by admin on Wed Apr 02 07:50:18 GMT 2025
PRIMARY
NIH
NCATS
PRIVACY NOTICE
ACCESSIBILITY
DISCLAIMER
HHS VULNERABILITY DISCLOSURE
For language access assistance, contact the NCATS Public Information Officer
National Center for Advancing Translational Sciences (NCATS),
6701 Democracy Boulevard, Bethesda MD 20892-4874 • 301-594-8966