U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
Duvalgagene Otiparvovec
INN  
Official Name English
4D-310
Preferred Name English
DUVALGAGENE OTIPARVOVEC [USAN]
Common Name English
duvalgagene otiparvovec [INN]
Common Name English
4D-C102
Code English
DNA (recombinant replication-defective adeno-associated virus 2 vector 4D-310 cytomegalovirus immediate-early enhancer element plus chicken ?-actin exon 1 plus intron 1 plus rabbit ?-globin splice acceptor plus human ?-galactosidase A codon-optimized gen
Common Name English
recombinant, non-replicating adeno-associated virus serotype 2 variant 4D-C102 (rAAV2 [4D-C102]) vector encoding codon optimized human alpha-galactosidase A (GLA) under control of a CAG promoter (cytomegalovirus (CMV) immediate-early enhancer/chicken ?-a
Common Name English
Code System Code Type Description
INN
12386
Created by admin on Wed Apr 02 08:40:19 GMT 2025 , Edited by admin on Wed Apr 02 08:40:19 GMT 2025
PRIMARY
FDA UNII
K24R94BC3K
Created by admin on Wed Apr 02 08:40:19 GMT 2025 , Edited by admin on Wed Apr 02 08:40:19 GMT 2025
PRIMARY
CAS
2768102-81-2
Created by admin on Wed Apr 02 08:40:19 GMT 2025 , Edited by admin on Wed Apr 02 08:40:19 GMT 2025
PRIMARY
NCI_THESAURUS
C206902
Created by admin on Wed Apr 02 08:40:19 GMT 2025 , Edited by admin on Wed Apr 02 08:40:19 GMT 2025
PRIMARY
USAN
NO-23
Created by admin on Wed Apr 02 08:40:19 GMT 2025 , Edited by admin on Wed Apr 02 08:40:19 GMT 2025
PRIMARY
SMS_ID
300000039586
Created by admin on Wed Apr 02 08:40:19 GMT 2025 , Edited by admin on Wed Apr 02 08:40:19 GMT 2025
PRIMARY
INN
12860
Created by admin on Wed Apr 02 08:40:19 GMT 2025 , Edited by admin on Wed Apr 02 08:40:19 GMT 2025
PRIMARY