U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
149124
Name Type Language
Alvamemugene Sulseparvovec
INN  
Official Name English
DNA (recombinant human adeno-associated virus AAV-LK03 vector LB-001 human methylmalonyl-coenzyme A mutase codon-optimized transgene plus porcine teschovirus 1 peptide 2A plus human albumin homology arms plus human adeno-associated virus 2 inverted termi
Preferred Name English
alvamemugene sulseparvovec [INN]
Common Name English
recombinant, non-replicating adeno-associated virus (rAAV) vector with a liver-trophic LK03 capsid, encoding codon-optimised human methylmalonyl-CoA mutase (MMUT, also referred to as MUT), preceded by the self-cleaving 2A-peptide of porcine teschovirus 1
Common Name English
Code System Code Type Description
INN
12220
Created by admin on Wed Apr 02 10:06:24 GMT 2025 , Edited by admin on Wed Apr 02 10:06:24 GMT 2025
PRIMARY
CAS
2640356-62-1
Created by admin on Wed Apr 02 10:06:24 GMT 2025 , Edited by admin on Wed Apr 02 10:06:24 GMT 2025
PRIMARY
SMS_ID
300000032093
Created by admin on Wed Apr 02 10:06:24 GMT 2025 , Edited by admin on Wed Apr 02 10:06:24 GMT 2025
PRIMARY
NCI_THESAURUS
C190453
Created by admin on Wed Apr 02 10:06:24 GMT 2025 , Edited by admin on Wed Apr 02 10:06:24 GMT 2025
PRIMARY
FDA UNII
HUH56XF3P7
Created by admin on Wed Apr 02 10:06:24 GMT 2025 , Edited by admin on Wed Apr 02 10:06:24 GMT 2025
PRIMARY
NIH
NCATS
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