U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
AT-845
Preferred Name English
Zocaglusagene Nuzaparvovec
USAN   INN  
Official Name English
AT845
Common Name English
DNA (recombinant adeno-associated virus vector AT845 mouse muscle-type creatine kinase enhancer plus mouse muscle-type creatine kinase promoter plus human lysosomal ?-glucosidase precursor codon-optimized transgene plus simian virus 40 polyadenylation si
Common Name English
zocaglusagene nuzaparvovec [INN]
Common Name English
Recombinant, non-replicating adeno-associated virus serotype 8 (rAAV8) vector encoding codon-optimized human acid alpha-glucosidase (GAA), also called lysosomal ?-glucosidase or acid maltase, under control of a mouse muscle creatine kinase (MCK) enhancer
Common Name English
ZOCAGLUSAGENE NUZAPARVOVEC [USAN]
Common Name English
Code System Code Type Description
FDA UNII
FDB4GQ8A3Y
Created by admin on Wed Apr 02 09:16:05 GMT 2025 , Edited by admin on Wed Apr 02 09:16:05 GMT 2025
PRIMARY
SMS_ID
300000044947
Created by admin on Wed Apr 02 09:16:05 GMT 2025 , Edited by admin on Wed Apr 02 09:16:05 GMT 2025
PRIMARY
CAS
2601264-52-0
Created by admin on Wed Apr 02 09:16:05 GMT 2025 , Edited by admin on Wed Apr 02 09:16:05 GMT 2025
PRIMARY
USAN
LM-146
Created by admin on Wed Apr 02 09:16:05 GMT 2025 , Edited by admin on Wed Apr 02 09:16:05 GMT 2025
PRIMARY
NCI_THESAURUS
C190444
Created by admin on Wed Apr 02 09:16:05 GMT 2025 , Edited by admin on Wed Apr 02 09:16:05 GMT 2025
PRIMARY
INN
12248
Created by admin on Wed Apr 02 09:16:05 GMT 2025 , Edited by admin on Wed Apr 02 09:16:05 GMT 2025
PRIMARY