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Approval Year

Unknown
149124
Name Type Language
Nefonadogene Vonzuparvovec
INN  
Official Name English
DNA (recombinant replication-defective adeno-associated virus 2 vector NFS02 human cytomegalovirus enhancer plus human cytomegalovirus promoter plus Macacine herpesvirus 3 chimeric intron plus human heme A farnesyltransferase gene COX10 mitochondrial tar
Preferred Name English
nefonadogene vonzuparvovec [INN]
Common Name English
recombinant, non-replicating adeno-associated virus serotype 2 (rAAV2) vector, encoding a mitochondrial targeting sequence from the human heme A farnesyltransferase gene (COX10) fused to codon-optimised human mitochondrial NADH dehydrogenase subunit 1 (M
Common Name English
Code System Code Type Description
CAS
2779554-99-1
Created by admin on Wed Apr 02 19:50:54 GMT 2025 , Edited by admin on Wed Apr 02 19:50:54 GMT 2025
PRIMARY
FDA UNII
FBB99Y9WCY
Created by admin on Wed Apr 02 19:50:54 GMT 2025 , Edited by admin on Wed Apr 02 19:50:54 GMT 2025
PRIMARY
INN
12868
Created by admin on Wed Apr 02 19:50:54 GMT 2025 , Edited by admin on Wed Apr 02 19:50:54 GMT 2025
PRIMARY
NCI_THESAURUS
C211770
Created by admin on Wed Apr 02 19:50:54 GMT 2025 , Edited by admin on Wed Apr 02 19:50:54 GMT 2025
PRIMARY
NIH
NCATS
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