U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
AT-001 (GENE THERAPY)
Preferred Name English
RESAMIRIGENE BILPARVOVEC
INN   USAN  
Official Name English
AT-132
Code English
RESAMIRIGENE BILPARVOVEC [USAN]
Common Name English
resamirigene bilparvovec [INN]
Common Name English
AT001 (GENE THERAPY)
Code English
AT132
Code English
A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 8 (AAV8) VECTOR EXPRESSING HUMAN MYOTUBULARIN 1 (MTM1), UNDER THE CONTROL OF THE HUMAN DESMIN GENE PROMOTER
Systematic Name English
Code System Code Type Description
USAN
EF-155
Created by admin on Wed Apr 02 08:09:56 GMT 2025 , Edited by admin on Wed Apr 02 08:09:56 GMT 2025
PRIMARY
CAS
2085240-27-1
Created by admin on Wed Apr 02 08:09:56 GMT 2025 , Edited by admin on Wed Apr 02 08:09:56 GMT 2025
PRIMARY
SMS_ID
100000182470
Created by admin on Wed Apr 02 08:09:56 GMT 2025 , Edited by admin on Wed Apr 02 08:09:56 GMT 2025
PRIMARY
NCI_THESAURUS
C177083
Created by admin on Wed Apr 02 08:09:56 GMT 2025 , Edited by admin on Wed Apr 02 08:09:56 GMT 2025
PRIMARY
FDA UNII
F6LOJ6ER4S
Created by admin on Wed Apr 02 08:09:56 GMT 2025 , Edited by admin on Wed Apr 02 08:09:56 GMT 2025
PRIMARY
INN
10920
Created by admin on Wed Apr 02 08:09:56 GMT 2025 , Edited by admin on Wed Apr 02 08:09:56 GMT 2025
PRIMARY