U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
139594
Name Type Language
Seglebegagene Dasniparvovec
INN  
Official Name English
DNA (recombinant replication-defective adeno-associated virus serotype hu68 vector PBGM01 human ubiquitin C promoter plus chimeric chicken β-actin and human β-globin intron plus human β-galactosidase codon-optimized gene GLB1 plus simian virus 40 poly
Common Name English
seglebegagene dasniparvovec [INN]
Common Name English
recombinant, non-replicating adeno-associated virus serotype hu68 (rAAVhu68) vector encoding codon-optimised human β-galactosidase (GLB1), under control of the human ubiquitin C promoter plus a chimeric intron, consisting of human β-globin splice donor
Common Name English
Code System Code Type Description
INN
12225
Created by admin on Sat Dec 16 18:38:09 GMT 2023 , Edited by admin on Sat Dec 16 18:38:09 GMT 2023
PRIMARY
NCI_THESAURUS
C190438
Created by admin on Sat Dec 16 18:38:09 GMT 2023 , Edited by admin on Sat Dec 16 18:38:09 GMT 2023
PRIMARY
CAS
2607029-99-0
Created by admin on Sat Dec 16 18:38:09 GMT 2023 , Edited by admin on Sat Dec 16 18:38:09 GMT 2023
PRIMARY
FDA UNII
EXB5VWG5TW
Created by admin on Sat Dec 16 18:38:09 GMT 2023 , Edited by admin on Sat Dec 16 18:38:09 GMT 2023
PRIMARY
NIH
NCATS
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