U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

2024
711
Name Type Language
Autologous CD34+ cells, containing hematopoietic stem cells (HSCs), transduced with a LVV encoding the human arylsulfatase A (ARSA) gene
Preferred Name English
Atidarsagene Autotemcel
INN   USAN  
Official Name English
Autologous CD34+ hematopoietic stem and progenitor cells transduced ex vivo with a replication-incompetent lentiviral vector encoding human arylsulfatase A (ARSA). Autologous CD34+ hematopoietic stem and progenitor cells (HSPC), obtained from bone marrow
Common Name English
atidarsagene autotemcel [INN]
Common Name English
ATIDARSAGENE AUTOTEMCEL [USAN]
Common Name English
OTL-200
Code English
Atidarsagene autotemcel [WHO-DD]
Common Name English
Code System Code Type Description
FDA UNII
EPP8G99QG4
Created by admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
PRIMARY
INN
11282
Created by admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
PRIMARY
USAN
JK-136
Created by admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
PRIMARY
NCI_THESAURUS
C180638
Created by admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
PRIMARY
SMS_ID
300000000100
Created by admin on Wed Apr 02 11:56:29 GMT 2025 , Edited by admin on Wed Apr 02 11:56:29 GMT 2025
PRIMARY
NIH
NCATS
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