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Approval Year

Unknown
149124
Name Type Language
Ciracigene golparvovec
Common Name English
Capsomere, recombinant adeno-associated virus clone rAAV-Olig-001 viral capsid protein VP1-VP2-VP3 complex (1:1:10), hexacontamer, complex with DNA (recombinant replication-defective adeno-associated virus vector cytomegalovirus enhancer plus chicken ?-a
Preferred Name English
recombinant, self-complementary non-replicating adenoassociated virus vector with Olig-001* capsid (rAAV-Olig-001) encoding codon-optimized human aspartoacylase (ASPA, ASP, ACY2) under control of a cytomegalovirus (CMV) enhancer/chicken ?-actin (CBh) hyb
Common Name English
ciracigene golparvovec [INN]
Common Name English
Code System Code Type Description
FDA UNII
DM5GA58Q2Z
Created by admin on Wed Apr 02 19:56:34 GMT 2025 , Edited by admin on Wed Apr 02 19:56:34 GMT 2025
PRIMARY
SMS_ID
300000044703
Created by admin on Wed Apr 02 19:56:34 GMT 2025 , Edited by admin on Wed Apr 02 19:56:34 GMT 2025
PRIMARY
INN
12885
Created by admin on Wed Apr 02 19:56:34 GMT 2025 , Edited by admin on Wed Apr 02 19:56:34 GMT 2025
PRIMARY
CAS
2847055-64-3
Created by admin on Wed Apr 02 19:56:34 GMT 2025 , Edited by admin on Wed Apr 02 19:56:34 GMT 2025
PRIMARY
NCI_THESAURUS
C206893
Created by admin on Wed Apr 02 19:56:34 GMT 2025 , Edited by admin on Wed Apr 02 19:56:34 GMT 2025
PRIMARY
NIH
NCATS
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