U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
DNA, d(P-thio)([2?,5?-anhydro-6?-deoxy-4?-C-(hydroxymethyl)-?-L-mannofurano]rA-(3??4?)-[2?,5?-anhydro-6?-deoxy-4?-C-(hydroxymethyl)-?-L-mannofurano]rA-(3??4?)-[2?,5?-anhydro-6?-deoxy-4?-C-(hydroxymethyl)-?-L-mannofurano]m5rU-A-A-T-m5C-T-m5C-A-T-G-T-(3??4
Preferred Name English
Bezeparsen
INN  
Official Name English
all-P-ambo-5'-O-(28-[(2-acetamido-2-deoxy-?-D -galactopyranosyl)oxy]-16,16-bis{[3-({6-[(2-acetamido-2-deoxy-?-D -galactopyranosyl)oxy]hexyl}amino)-3-oxopropoxy]methyl}-1-hydroxy-1,10,14,21-tetraoxo-2,18-dioxa-9,15,22-triaza-1? 5 -phosphaoctacosan-1-yl)-2
Common Name English
bezeparsen [INN]
Common Name English
Code System Code Type Description
NCI_THESAURUS
C190429
Created by admin on Tue Apr 01 22:56:22 GMT 2025 , Edited by admin on Tue Apr 01 22:56:22 GMT 2025
PRIMARY
FDA UNII
CP66E80XXT
Created by admin on Tue Apr 01 22:56:22 GMT 2025 , Edited by admin on Tue Apr 01 22:56:22 GMT 2025
PRIMARY
CAS
2639640-84-7
Created by admin on Tue Apr 01 22:56:22 GMT 2025 , Edited by admin on Tue Apr 01 22:56:22 GMT 2025
PRIMARY
INN
12322
Created by admin on Tue Apr 01 22:56:22 GMT 2025 , Edited by admin on Tue Apr 01 22:56:22 GMT 2025
PRIMARY
Sugar Site Range Site Count
1_1-1_3;1_14-1_16 6 / 16
Deoxyribose (DNA) 1_4-1_13 10 / 16
Linkage Site Range Site Count
Phosporothioate 1_1-1_15 15 / 15