U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS
This repository is under review for potential modification in compliance with Administration directives.

Details

Stereochemistry ABSOLUTE
Molecular Formula C32H39N7O4S
Molecular Weight 617.762
Optical Activity UNSPECIFIED
Defined Stereocenters 1 / 1
E/Z Centers 0
Charge 0

SHOW SMILES / InChI
Structure of Vanzacaftor

SMILES

CC1(C)C[C@H]2CN1C3=NC(=CC=C3C(=O)NS(=O)(=O)C4=NC(NCCC2)=CC=C4)N5C=CC(OCCC6C7(CC7)C68CC8)=N5

InChI

InChIKey=VCSUIBJKYCVWNF-NRFANRHFSA-N
InChI=1S/C32H39N7O4S/c1-30(2)19-21-5-4-16-33-24-6-3-7-27(34-24)44(41,42)37-29(40)22-8-9-25(35-28(22)38(30)20-21)39-17-10-26(36-39)43-18-11-23-31(12-13-31)32(23)14-15-32/h3,6-10,17,21,23H,4-5,11-16,18-20H2,1-2H3,(H,33,34)(H,37,40)/t21-/m0/s1

HIDE SMILES / InChI

Approval Year

Name Type Language
VX-121
Preferred Name English
Vanzacaftor
INN   USAN  
Official Name English
vanzacaftor [INN]
Common Name English
VANZACAFTOR [USAN]
Common Name English
13H-17,20-Methano-8,12-nitrilo-12H-pyrido[3,2-d][1,2,6,13]thiatriazacyclooctadecin-5(6H)-one, 2-[3-(2-dispiro[2.0.2.1]hept-7-ylethoxy)-1H-pyrazol-1-yl]-14,15,16,17,18,19-hexahydro-19,19-dimethyl-, 7,7-dioxide, (17S)-
Systematic Name English
Classification Tree Code System Code
FDA ORPHAN DRUG 777220
Created by admin on Wed Apr 02 04:13:13 GMT 2025 , Edited by admin on Wed Apr 02 04:13:13 GMT 2025
Code System Code Type Description
SMS_ID
300000046984
Created by admin on Wed Apr 02 04:13:13 GMT 2025 , Edited by admin on Wed Apr 02 04:13:13 GMT 2025
PRIMARY
USAN
LM-135
Created by admin on Wed Apr 02 04:13:13 GMT 2025 , Edited by admin on Wed Apr 02 04:13:13 GMT 2025
PRIMARY
CAS
2374124-49-7
Created by admin on Wed Apr 02 04:13:13 GMT 2025 , Edited by admin on Wed Apr 02 04:13:13 GMT 2025
PRIMARY
PUBCHEM
139399801
Created by admin on Wed Apr 02 04:13:13 GMT 2025 , Edited by admin on Wed Apr 02 04:13:13 GMT 2025
PRIMARY
INN
11971
Created by admin on Wed Apr 02 04:13:13 GMT 2025 , Edited by admin on Wed Apr 02 04:13:13 GMT 2025
PRIMARY
NCI_THESAURUS
C188560
Created by admin on Wed Apr 02 04:13:13 GMT 2025 , Edited by admin on Wed Apr 02 04:13:13 GMT 2025
PRIMARY
FDA UNII
COM1POP492
Created by admin on Wed Apr 02 04:13:13 GMT 2025 , Edited by admin on Wed Apr 02 04:13:13 GMT 2025
PRIMARY