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Approval Year

Unknown
149124
Name Type Language
autologous CD34+ hematopoietic stem and progenitor cells (HSPCs) obtained from peripheral blood by leukapheresis, genetically modified ex vivo by electroporation of a guide RNA (gRNA) that targets the two ?-globin gene (HBG1 and HBG2) promotors and a mes
Preferred Name English
Ristoglogene Autogetemcel
INN  
Official Name English
ristoglogene autogetemcel [INN]
Common Name English
Code System Code Type Description
FDA UNII
CEL7E4NG36
Created by admin on Wed Apr 02 18:18:56 GMT 2025 , Edited by admin on Wed Apr 02 18:18:56 GMT 2025
PRIMARY
INN
13397
Created by admin on Wed Apr 02 18:18:56 GMT 2025 , Edited by admin on Wed Apr 02 18:18:56 GMT 2025
PRIMARY
NIH
NCATS
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