U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
BIIB-080
Preferred Name English
Diranersen
INN  
Official Name English
all-P-ambo-2'-O-(2-methoxyethyl)-5-methyl-P-thiocytidylyl-(3'?5')-2'-O-(2-methoxyethyl)-5-methylcytidylyl-(3'?5')-2'-O-(2-methoxyethyl)-P-thioguanylyl-(3'?5')-2'-O-(2-methoxyethyl)-5-methyl-P-thiouridylyl-(3'?5')-2'-O-(2-methoxyethyl)-5-methyl-Pthiouridy
Common Name English
BIIB080
Code English
RNA, ([2?-O-(2-methoxyethyl)]m5C-sp-[2?-O-(2-methoxyethyl)]m5C-[2?-O-(2-methoxyethyl)]G-sp-[2?-O-(2-methoxyethyl)]m5U-sp-[2?-O-(2-methoxyethyl)]m5U-sp-dT-sp-dT-sp-m5dC-sp-dT-sp-dT-sp-dA-sp-m5dC-sp-m5dC-sp-[2?-O-(2-methoxyethyl)]A-sp-[2?-O-(2-methoxyethyl
Common Name English
diranersen [INN]
Common Name English
Code System Code Type Description
FDA UNII
96J3L33PWD
Created by admin on Wed Apr 02 12:37:12 GMT 2025 , Edited by admin on Wed Apr 02 12:37:12 GMT 2025
PRIMARY
CAS
2304711-06-4
Created by admin on Wed Apr 02 12:37:12 GMT 2025 , Edited by admin on Wed Apr 02 12:37:12 GMT 2025
PRIMARY
INN
13317
Created by admin on Wed Apr 02 12:37:12 GMT 2025 , Edited by admin on Wed Apr 02 12:37:12 GMT 2025
PRIMARY
SMS_ID
300000013142
Created by admin on Wed Apr 02 12:37:12 GMT 2025 , Edited by admin on Wed Apr 02 12:37:12 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_6-1_13 8 / 18
2'-O-Methoxyethyl ribose 1_1-1_5;1_14-1_18 10 / 18
Linkage Site Range Site Count
Phosporothioate 1_2;1_4-1_15;1_17-1_18 15 / 17
Phosphate 1_3;1_16 2 / 17