U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
AAV8G6PASE
Preferred Name English
Pariglasgene Brecaparvovec
USAN   INN  
Official Name English
DTX401
Code English
AAV8G6PC
Code English
pariglasgene brecaparvovec [INN]
Common Name English
DNA (recombinant adeno-associated virus 8 vector DTX401 human glucose 6-phosphatase ? codon-optimized gene G6PC plus adeno-associated virus 2 inverted terminal repeat flanks)
Common Name English
PARIGLASGENE BRECAPARVOVEC [USAN]
Common Name English
A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRAL VECTOR SEROTYPE 8 (RAAV8), ENCODING CODON-OPTIMIZED HUMAN GLUCOSE-6-PHOSPHATASE (G6PC) UNDER THE CONTROL OF THE NATIVE HUMAN G6PC PROMOTER/ENHANCER AND AN SV40 POLYADENYLATION SEQUENCE, CONTAINING A CH
Common Name English
DTX-401
Code English
Code System Code Type Description
NCI_THESAURUS
C177070
Created by admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
PRIMARY
USAN
NO-20
Created by admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
PRIMARY
CAS
2259927-72-3
Created by admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
PRIMARY
SMS_ID
100000183200
Created by admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
PRIMARY
USAN
NO-20
Created by admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
PRIMARY
INN
11440
Created by admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
PRIMARY
FDA UNII
7LP92X4WPE
Created by admin on Wed Apr 02 07:38:45 GMT 2025 , Edited by admin on Wed Apr 02 07:38:45 GMT 2025
PRIMARY