U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
renadirsen [INN]
Preferred Name English
Renadirsen
INN  
Official Name English
RNA, (P-thio)([2?,6?-anhydro-5?-deoxy-4?-C-(hydroxymethyl)-?-L-lyxo-hexofurano]m5C-Gm-(3??4?)-[2?,6?-anhydro-5?-deoxy-4?-C-(hydroxymethyl)-?-L-lyxo-hexofurano]m5C-(3??4?)-[2?,6?-anhydro-5?-deoxy-4?-C-(hydroxymethyl)-?-L-lyxo-hexofurano]m5U-Gm-Cm-(3??4?)-
Systematic Name English
RENAPERSEN
Common Name English
Classification Tree Code System Code
NCI_THESAURUS C78281
Created by admin on Wed Apr 02 19:17:22 GMT 2025 , Edited by admin on Wed Apr 02 19:17:22 GMT 2025
Code System Code Type Description
FDA UNII
4RW6WRD7SW
Created by admin on Wed Apr 02 19:17:22 GMT 2025 , Edited by admin on Wed Apr 02 19:17:22 GMT 2025
PRIMARY
SMS_ID
300000005921
Created by admin on Wed Apr 02 19:17:22 GMT 2025 , Edited by admin on Wed Apr 02 19:17:22 GMT 2025
PRIMARY
NCI_THESAURUS
C152190
Created by admin on Wed Apr 02 19:17:22 GMT 2025 , Edited by admin on Wed Apr 02 19:17:22 GMT 2025
PRIMARY
PUBCHEM
131801099
Created by admin on Wed Apr 02 19:17:22 GMT 2025 , Edited by admin on Wed Apr 02 19:17:22 GMT 2025
PRIMARY
CAS
1782108-31-9
Created by admin on Wed Apr 02 19:17:22 GMT 2025 , Edited by admin on Wed Apr 02 19:17:22 GMT 2025
PRIMARY
INN
10371
Created by admin on Wed Apr 02 19:17:22 GMT 2025 , Edited by admin on Wed Apr 02 19:17:22 GMT 2025
PRIMARY
Sugar Site Range Site Count
2'-O,4'-ethylene bridged Ribose 1_1;1_3-1_4;1_7-1_8;1_11;1_13-1_14;1_17-1_18 10 / 18
2'-O-Methyl-Ribose 1_2;1_5-1_6;1_9-1_10;1_12;1_15-1_16 8 / 18
Linkage Site Range Site Count
Phosporothioate 1_2-1_18 17 / 17