U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
149124
Name Type Language
EDIT-101
Preferred Name English
Brinretigene Vesgedparvovec
INN  
Official Name English
DNA (recombinant adeno-associated virus vector EDIT-101 human U6 promoter plus nephrocystin 6 intron 26-specific CEP290-323 guide RNA gene plus human U6 promoter plus nephrocystin 6 intron 26-specific CEP290-64 guide RNA gene plus human rhodopsin kinase
Common Name English
brinretigene vesgedparvovec [INN]
Common Name English
Recombinant, non-replicating adeno-associated virus serotype 5 (rAAV5) vector encoding (1) codon-optimized Staphylococcus aureus clustered regularly interspaced short palindromic repeats (CRISPR)-associated protein 9 (Cas9) flanked by simian virus 40 (SV
Common Name English
Code System Code Type Description
FDA UNII
4G7DT7PP3L
Created by admin on Wed Apr 02 17:59:15 GMT 2025 , Edited by admin on Wed Apr 02 17:59:15 GMT 2025
PRIMARY
INN
12734
Created by admin on Wed Apr 02 17:59:15 GMT 2025 , Edited by admin on Wed Apr 02 17:59:15 GMT 2025
PRIMARY
NCI_THESAURUS
C203111
Created by admin on Wed Apr 02 17:59:15 GMT 2025 , Edited by admin on Wed Apr 02 17:59:15 GMT 2025
PRIMARY
CAS
2768756-11-0
Created by admin on Wed Apr 02 17:59:15 GMT 2025 , Edited by admin on Wed Apr 02 17:59:15 GMT 2025
PRIMARY
SMS_ID
300000008865
Created by admin on Wed Apr 02 17:59:15 GMT 2025 , Edited by admin on Wed Apr 02 17:59:15 GMT 2025
PRIMARY
NIH
NCATS
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