U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
139594
Name Type Language
Brinretigene Vesgedparvovec
INN  
Official Name English
EDIT-101
Code English
DNA (recombinant adeno-associated virus vector EDIT-101 human U6 promoter plus nephrocystin 6 intron 26-specific CEP290-323 guide RNA gene plus human U6 promoter plus nephrocystin 6 intron 26-specific CEP290-64 guide RNA gene plus human rhodopsin kinase
Common Name English
brinretigene vesgedparvovec [INN]
Common Name English
Recombinant, non-replicating adeno-associated virus serotype 5 (rAAV5) vector encoding (1) codon-optimized Staphylococcus aureus clustered regularly interspaced short palindromic repeats (CRISPR)-associated protein 9 (Cas9) flanked by simian virus 40 (SV
Common Name English
Code System Code Type Description
FDA UNII
4G7DT7PP3L
Created by admin on Sat Dec 16 19:59:40 GMT 2023 , Edited by admin on Sat Dec 16 19:59:40 GMT 2023
PRIMARY
INN
12734
Created by admin on Sat Dec 16 19:59:40 GMT 2023 , Edited by admin on Sat Dec 16 19:59:40 GMT 2023
PRIMARY
CAS
2768756-11-0
Created by admin on Sat Dec 16 19:59:40 GMT 2023 , Edited by admin on Sat Dec 16 19:59:40 GMT 2023
PRIMARY
NIH
NCATS
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