DNA (recombinant adeno-associated virus vector EDIT-101 human U6 promoter plus nephrocystin 6 intron 26-specific CEP290-323 guide RNA gene plus human U6 promoter plus nephrocystin 6 intron 26-specific CEP290-64 guide RNA gene plus human rhodopsin kinase
Common Name
English
brinretigene vesgedparvovec [INN]
Common Name
English
Recombinant, non-replicating adeno-associated virus serotype 5 (rAAV5) vector encoding (1) codon-optimized Staphylococcus aureus clustered regularly interspaced short palindromic repeats (CRISPR)-associated protein 9 (Cas9) flanked by simian virus 40 (SV
