A RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRAL VECTOR SEROTYPE 6 (AAV6) ENCODING CODON-OPTIMISED HUMAN ALPHA-GALACTOSIDASE A (GLA) UNDER CONTROL OF LIVER-SPECIFIC REGULATORY ELEMENTS (COMPRISING ENHANCER AND HEPATIC CONTROL REGION FROM THE HUMAN A
Common Name
English
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR ST-920 LIVER-SPECIFIC ENHANCER-PROMOTER-INTRON REGULATORY MODULE PLUS HUMAN .ALPHA.-GALACTOSIDASE PRECURSOR-SPECIFYING)
