U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
Mivelsiran
INN  
Official Name English
mivelsiran [INN]
Common Name English
RNA, ((5′,6′-dideoxy-6′-phosphono-β-D-ribo-hex-5-enofurano)Um-sp-(2′-deoxy-2′-fluoro)U-sp-Am-Gm-Gm-Um-(3′→3′)-[1-de-β-D-ribofuranosyl-1-[(2S)-2,3-dihydroxypropyl]]m5U-(2′→5′)-Gm-Gm-Am-Um-dT-Um-(2′-deoxy-2′-fluoro)U-Cm-dG-Um-Am
Common Name English
Code System Code Type Description
FDA UNII
39CFL75KXH
Created by admin on Sat Dec 16 19:11:03 GMT 2023 , Edited by admin on Sat Dec 16 19:11:03 GMT 2023
PRIMARY
INN
12750
Created by admin on Sat Dec 16 19:11:03 GMT 2023 , Edited by admin on Sat Dec 16 19:11:03 GMT 2023
PRIMARY
CAS
2572991-83-2
Created by admin on Sat Dec 16 19:11:03 GMT 2023 , Edited by admin on Sat Dec 16 19:11:03 GMT 2023
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_12;1_16;2_9;2_11 4 / 44
2'-O-Methyl-Ribose 1_1;1_3-1_11;1_13;1_15;1_17-1_23;2_1-2_8;2_10;2_12-2_21 38 / 44
2'-Fluoro-Ribose 1_2;1_14 2 / 44
Linkage Site Range Site Count
Phosporothioate 1_2-1_3;1_22-1_23;2_2-2_3;2_20-2_21 8 / 42
Phosphate 1_4-1_21;2_4-2_19 34 / 42