U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
IONIS-FB-LRX
Preferred Name English
Sefaxersen Sodium
USAN  
Official Name English
ISIS-696844
Code English
ISIS-696844 SODIUM
Code English
all-P-ambo-5?-O-{[(6-{5-[(tris{3-[6-(2-acetamido-2-deoxy-?-D-galactopyranosyloxy)hexylamino]-3-oxopropoxymethyl})methyl]amino-5-oxopentanamido}hexyl)]phospho}-2?-O-(2-methoxyethyl)-P-thioadenylyl-(3?-O?5?-O)-2?-O-(2-methoxyethyl)-5-methyl-P-thiouridylyl-
Systematic Name English
DNA, d(P-thio)([2?-O-(2-methoxyethyl)]rA-[2?-O-(2-methoxyethyl)]m5rU-[2?-O-( 2-methoxyethyl)]m5rC-[2?-O-(2-methoxyethyl)]m5rC-[2?-O-(2-methoxyethyl) ]m5rC-A-m5C-G-m5C-m5C-m5C-m5C-T-G-T-[2?-O-(2-methoxyethyl)]m5rC-[2?-O-( 2-methoxyethyl)]m5rC-[2?-O-(2-met
Systematic Name English
SEFAXERSEN SODIUM [USAN]
Common Name English
Code System Code Type Description
NCI_THESAURUS
C203036
Created by admin on Wed Apr 02 04:02:48 GMT 2025 , Edited by admin on Wed Apr 02 04:02:48 GMT 2025
PRIMARY
FDA UNII
37KI8XF3IH
Created by admin on Wed Apr 02 04:02:48 GMT 2025 , Edited by admin on Wed Apr 02 04:02:48 GMT 2025
PRIMARY
SMS_ID
300000049051
Created by admin on Wed Apr 02 04:02:48 GMT 2025 , Edited by admin on Wed Apr 02 04:02:48 GMT 2025
PRIMARY
USAN
KL-234
Created by admin on Wed Apr 02 04:02:48 GMT 2025 , Edited by admin on Wed Apr 02 04:02:48 GMT 2025
PRIMARY
CAS
2272983-11-4
Created by admin on Wed Apr 02 04:02:48 GMT 2025 , Edited by admin on Wed Apr 02 04:02:48 GMT 2025
PRIMARY
Sugar Site Range Site Count
Deoxyribose (DNA) 1_6-1_15 10 / 20
2'-O-Methoxyethyl ribose 1_1-1_5;1_16-1_20 10 / 20
Linkage Site Range Site Count
Sodium Phosporothioate 1_1-1_19 19 / 19