U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
TOMLIGISIRAN
INN  
Official Name English
RNA, ((1'-DE(6-AMINO-9H-PURIN-9-YL))DA-(5'->5')-CM-GM-CM-UM-GM-UM-AM-GM-(2'-DEOXY-2'-FLUORO)G-(2'-DEOXY-2'-FLUORO)C-(2'-DEOXY-2'-FLUORO)A-UM-AM-AM-AM-UM-UM-GM-GM-UM-AM-(3'->3')-SP-(1'-DE(6-AMINO-9H-PURIN-9-YL))DA), 3'-(O-(CIS-4-((3S,8S)-17-((2-(ACETYLAMI
Common Name English
tomligisiran [INN]
Common Name English
Code System Code Type Description
FDA UNII
35S90A5FLO
Created by admin on Sat Dec 16 15:11:29 UTC 2023 , Edited by admin on Sat Dec 16 15:11:29 UTC 2023
PRIMARY
CAS
2202789-48-6
Created by admin on Sat Dec 16 15:11:29 UTC 2023 , Edited by admin on Sat Dec 16 15:11:29 UTC 2023
PRIMARY
INN
11469
Created by admin on Sat Dec 16 15:11:29 UTC 2023 , Edited by admin on Sat Dec 16 15:11:29 UTC 2023
PRIMARY INN
NCI_THESAURUS
C179127
Created by admin on Sat Dec 16 15:11:29 UTC 2023 , Edited by admin on Sat Dec 16 15:11:29 UTC 2023
PRIMARY
Sugar Site Range Site Count
2'-Fluoro-Ribose 1_9-1_11;2_2;2_4;2_6;2_8;2_10;2_12;2_14;2_16;2_18 12 / 42
2'-O-Methyl-Ribose 1_1-1_8;1_12-1_21;2_1;2_3;2_5;2_7;2_9;2_11;2_13;2_15;2_17;2_19-2_21 30 / 42
Linkage Site Range Site Count
Phosporothioate 2_2-2_4;2_21 4 / 40
Phosphate 1_2-1_21;2_5-2_20 36 / 40