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Approval Year

Unknown
149124
Name Type Language
Pasemnogene Gleparvovec
INN  
Official Name English
Capsomere, recombinant adeno-associated virus 9 viral capsid protein VP1 [422-tryptophan,446-phenylalanine] complex with viral capsid protein VP2 [285-tryptophan,309-phenylalanine] complex with viral capsid protein VP3 [220-tryptophan,244-phenylalanine]
Preferred Name English
recombinant non-replicating adeno-associated virus serotype 9 (AAV9) vector, encoding a codon-optimised human survival of motor neuron 1 (SMN1) gene, under control of the cytomegalovirus (CMV) enhancer/promoter and terminated by a human growth hormone po
Common Name English
pasemnogene gleparvovec [INN]
Common Name English
Code System Code Type Description
FDA UNII
2Q4YZ4G35L
Created by admin on Wed Apr 02 20:08:45 GMT 2025 , Edited by admin on Wed Apr 02 20:08:45 GMT 2025
PRIMARY
CAS
2913126-89-1
Created by admin on Wed Apr 02 20:08:45 GMT 2025 , Edited by admin on Wed Apr 02 20:08:45 GMT 2025
PRIMARY
NCI_THESAURUS
C211721
Created by admin on Wed Apr 02 20:08:45 GMT 2025 , Edited by admin on Wed Apr 02 20:08:45 GMT 2025
PRIMARY
NIH
NCATS
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