DNA (recombinant replication-defective adeno-associated virus serotype 9 vector UX701 murine transthyretin enhancer plus human transthyretin promoter plus simian virus 40 intron plus human adenosine triphosphatase copper-transporting ? metal-binding doma
Common Name
English
recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector encoding ATPase copper-transporting beta gene (ATP7B, copper transporting ATPase 2), modified to encode the last three of the six metal-binding domains (ATP7B-MBD456), under co