U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
139594
Name Type Language
Rivunatpagene Miziparvovec
INN  
Official Name English
DNA (recombinant replication-defective adeno-associated virus serotype 9 vector UX701 murine transthyretin enhancer plus human transthyretin promoter plus simian virus 40 intron plus human adenosine triphosphatase copper-transporting β metal-binding dom
Common Name English
recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector encoding ATPase copper-transporting beta gene (ATP7B, copper transporting ATPase 2), modified to encode the last three of the six metal-binding domains (ATP7B-MBD456), under co
Common Name English
rivunatpagene miziparvovec [INN]
Common Name English
UX-701
Common Name English
UX701
Code English
Code System Code Type Description
FDA UNII
24Q8LJQ6Y2
Created by admin on Sat Dec 16 18:22:35 GMT 2023 , Edited by admin on Sat Dec 16 18:22:35 GMT 2023
PRIMARY
CAS
2646715-00-4
Created by admin on Sat Dec 16 18:22:35 GMT 2023 , Edited by admin on Sat Dec 16 18:22:35 GMT 2023
PRIMARY
INN
12388
Created by admin on Sat Dec 16 18:22:35 GMT 2023 , Edited by admin on Sat Dec 16 18:22:35 GMT 2023
PRIMARY
NCI_THESAURUS
C189971
Created by admin on Sat Dec 16 18:22:35 GMT 2023 , Edited by admin on Sat Dec 16 18:22:35 GMT 2023
PRIMARY
NIH
NCATS
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