U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Unknown
149124
Name Type Language
UX701
Preferred Name English
Rivunatpagene Miziparvovec
INN   USAN  
Official Name English
DNA (recombinant replication-defective adeno-associated virus serotype 9 vector UX701 murine transthyretin enhancer plus human transthyretin promoter plus simian virus 40 intron plus human adenosine triphosphatase copper-transporting ? metal-binding doma
Common Name English
recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector encoding ATPase copper-transporting beta gene (ATP7B, copper transporting ATPase 2), modified to encode the last three of the six metal-binding domains (ATP7B-MBD456), under co
Common Name English
rivunatpagene miziparvovec [INN]
Common Name English
UX-701
Common Name English
RIVUNATPAGENE MIZIPARVOVEC [USAN]
Common Name English
Code System Code Type Description
SMS_ID
300000023114
Created by admin on Wed Apr 02 10:55:02 GMT 2025 , Edited by admin on Wed Apr 02 10:55:02 GMT 2025
PRIMARY
FDA UNII
24Q8LJQ6Y2
Created by admin on Wed Apr 02 10:55:02 GMT 2025 , Edited by admin on Wed Apr 02 10:55:02 GMT 2025
PRIMARY
CAS
2646715-00-4
Created by admin on Wed Apr 02 10:55:02 GMT 2025 , Edited by admin on Wed Apr 02 10:55:02 GMT 2025
PRIMARY
INN
12388
Created by admin on Wed Apr 02 10:55:02 GMT 2025 , Edited by admin on Wed Apr 02 10:55:02 GMT 2025
PRIMARY
USAN
MN-21
Created by admin on Wed Apr 02 10:55:02 GMT 2025 , Edited by admin on Wed Apr 02 10:55:02 GMT 2025
PRIMARY
NCI_THESAURUS
C189971
Created by admin on Wed Apr 02 10:55:02 GMT 2025 , Edited by admin on Wed Apr 02 10:55:02 GMT 2025
PRIMARY
NIH
NCATS
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