U.S. Department of Health & Human Services Divider Arrow National Institutes of Health Divider Arrow NCATS

Approval Year

Name Type Language
NEDOSIRAN
INN   USAN  
Official Name English
nedosiran [INN]
Common Name English
Nedosiran [WHO-DD]
Common Name English
NEDOSIRAN [USAN]
Common Name English
RNA, (AM-SP-UM-(2'-DEOXY-2'-FLUORO)G-UM-(2'-DEOXY-2'-FLUORO)U-GM-UM-(2'-DEOXY-2'-FLUORO)C-(2'-DEOXY-2'-FLUORO)C-(2'-DEOXY-2'-FLUORO)U-(2'-DEOXY-2'-FLUORO)U-UM-(2'-DEOXY-2'-FLUORO)U-UM-(2'-DEOXY-2'-FLUORO)A-UM-(2'-DEOXY-2'-FLUORO)C-UM-GM-AM-GM-CM-AM-GM-CM
Systematic Name English
DCR-PHXC FREE ACID
Code English
Code System Code Type Description
CAS
2266591-83-5
Created by admin on Sat Dec 16 15:05:34 UTC 2023 , Edited by admin on Sat Dec 16 15:05:34 UTC 2023
PRIMARY
USAN
HI-158
Created by admin on Sat Dec 16 15:05:34 UTC 2023 , Edited by admin on Sat Dec 16 15:05:34 UTC 2023
PRIMARY
FDA UNII
13U9R5J3WL
Created by admin on Sat Dec 16 15:05:34 UTC 2023 , Edited by admin on Sat Dec 16 15:05:34 UTC 2023
PRIMARY
NCI_THESAURUS
C175828
Created by admin on Sat Dec 16 15:05:34 UTC 2023 , Edited by admin on Sat Dec 16 15:05:34 UTC 2023
PRIMARY
INN
11373
Created by admin on Sat Dec 16 15:05:34 UTC 2023 , Edited by admin on Sat Dec 16 15:05:34 UTC 2023
PRIMARY
Sugar Site Range Site Count
2'-Fluoro-Ribose 1_2-1_5;1_7;1_9-1_10;1_14;1_16;1_18;2_3;2_5;2_8-2_11;2_13;2_15;2_17 19 / 58
2'-O-Methyl-Ribose 1_1;1_6;1_8;1_11-1_13;1_15;1_17;1_19-1_22;2_1-2_2;2_4;2_6-2_7;2_12;2_14;2_16;2_18-2_26;2_31-2_36 35 / 58
D-Ribose (RNA) 2_27-2_30 4 / 58
Linkage Site Range Site Count
Phosporothioate 1_1-1_3;1_20-1_21;2_1 6 / 56
Phosphate 1_4-1_19;2_2-2_35 50 / 56